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… Webinar: Economic Modelling Challenges in Rare Diseases Share on: … 2019 Watch the recording When seeking approval for rare disease products, demonstrating value for therapies can be a …
… Health Economics More than ever, health economic information affects how patients, providers, payers … indications Determine health economic endpoints for your clinical trials Analyze economic data collected in clinical … studies include: Study Type Description Burden of Illness Disease incidence and prevalence; real-world outcomes; costs …
… Decision-analytic models provide a framework for compiling clinical and economic evidence in a systematic fashion, … (individual patient, discrete-event, etc.) Communicable disease models Linear, integer, and non-linear mathematical … analysis Our Approach From design to deliverables, publications , and ongoing support, we develop and validate …
… Economic Qualitative Inquiry, Policy, and Access Our focused … about your new product, we can help you understand the clinical and economic evidence they will expect to see for … boards to address negative coverage policies in the US and disease area concerns worldwide. To get a well-rounded view …
… FDA Rare Disease Day 2024 Virtual Public Meeting Share on: Friday, … of certain groups of otherwise eligible subjects in clinical trials. This panel also includes discussion of … Sclerosis Act (ACT for ALS) initiative. Romano shares, “I am truly honored to facilitate the Patient Committee as …
… Benefit-Risk Assessment Do your product’s benefits outweigh its potential risks? More importantly, do … a strategy for possible new studies to include in your clinical development program and clarify appropriate … in the same way in both short and long-term studies or using the same units. By engaging with our team early in the …
… Clinical Trials With broad therapeutic experience across all … (QoL) assessments may be used to demonstrate additional benefits to patients and provide compelling evidence for … clinical and patient-centered outcomes Assessing burden of disease Exploring the impact of missing data We will …
… how your patients and other decision-makers perceive the benefits of your treatment features and their tolerance for … Benefit-risk preference studies demonstrate the net benefits of treatments by quantifying the relative importance of benefits and risks and a patient’s maximum acceptable risk …
… needed - Plan for the collection of utility data within a clinical trial and product R&D program Measurement - Develop … - Perform mapping to derive EQ-5D utility estimates from a disease-specific measure - Develop a health preference index … such as NICE, SMC, CDR, and PBAC), value messaging , and publications A Team Approach Let our multidisciplinary team …
… Rare Diseases A Wealth of Experience We have collaborated with our clients on projects to research rare diseases, rare disease treatment, and complications and comorbidities of …