Peay HL, Fischer R, Mange B, Paquin RS, Smith EC, Sadosky A, Russo L, Ricotti V, Rensch C, Morris C, Martin AS, Ganot A, Beaverson K, Mansfield C. Patients' and caregivers' maximum acceptable risk of death for non-curative gene therapy to treat Duchenne muscular dystrophy. Mol Genet Genomic Med. 2021 May;9(5):e1664. doi: 10.1002/mgg3.1664
Martin AV, Coffield K. Hemophilia: information for educators and communication disorders specialists. Poster presented at the American Speech-Language-Hearing Association; April 1997. [abstract] Perspect Lang Learn Educ. 1997 Apr; 4:13-5.