Andrews S, Mansfield C, O'Neill C, Peay H. Meaningful treatment outcomes for Sanfilippo syndrome: using a combination of focus groups and best-worst scaling to elicit and explore parents' priorities. Poster presented at the 2019 25th Annual Qualitative Health Research Conference; October 2019. Vancouver, Canada. [abstract] Int J Qual Methods. 2020 Mar 30; 19:2. doi: 10.1177/1609406920909934
Ward A, Caro JJ, Green T, Huybrechts K, Arana A, Wait S, Eleftheriou A. An international survey of patients with thalassemia major and their views about sustaining life-long desferrioxamine use. BMC Clin Pharmacol. 2002;2(3).