Slota C, Bevans M, Yang L, Shrader J, Joe G, Carrillo N. Patient reported outcomes in GNE myopathy: incorporating a valid assessment of physical function in a rare disease. Disabil Rehabil. 2018 May;40(10):1206-13. doi: 10.1080/09638288.2017.1283712
Hauber B, Candrilli S, Snyder EH, McBurney CR. Validation of a model to assess long-term disease progression in Alzheimer's disease patients treated with rivastigmine. Neurobiol Aging. 2004 Jan 1;25:S136.